VISTAS

  • Research type

    Research Study

  • Full title

    A Randomized Double-Blind Placebo-Controlled Study to Evaluate the Efficacy and Safety of Volixibat in the Treatment of Cholestatic Pruritus in Patients with Primary Sclerosing Cholangitis (VISTAS)

  • IRAS ID

    289588

  • Contact name

    Lara Longpre

  • Contact email

    llongpre@mirumpharma.com

  • Sponsor organisation

    Mirum Pharmaceutical Inc

  • Eudract number

    2020-003027-41

  • Clinicaltrials.gov Identifier

    NCT04663308

  • Clinicaltrials.gov Identifier

    IND Number, 145022

  • Duration of Study in the UK

    4 years, 2 months, 1 days

  • Research summary

    PSC is a progressive inflammatory cholestatic disease characterised by inflammation and fibrosis of the bile ducts and liver. Intense pruritus (itching) can be a debilitating complication of certain cholestatic diseases and is likely a result of high circulating bile acid levels, which can lead to fatigue, social isolation, and a lower quality of life. Intractable pruritus can be the primary indication for liver transplantation. Frequently, PSC is commonly associated with inflammatory bowel disease (IBD). This study is to monitor the efficacy and safety in patients with primary sclerosing cholangitis (PSC).

    Male and female participants who are over 18 and have been identified as having or possibly having pruritus (itching) associated with primary sclerosing cholangitis (PSC) are being invited to take part in this study.

    This study will be conducted at multiple sites across North America and Europe, with other regions added as necessary.

    Participation in the Core Study is expected to last for approximately 32 weeks, including the screening period and Core Study period, with the option to continue into the Open Label Extension for 24 months.

  • REC name

    East of England - Cambridge South Research Ethics Committee

  • REC reference

    21/EE/0079

  • Date of REC Opinion

    19 May 2021

  • REC opinion

    Further Information Favourable Opinion