Transition care for Silver-Russell and Temple syndrome

  • Research type

    Research Study

  • Full title

    Building knowledge for transition and care into adulthood for patients with Silver-Russell and Temple Syndrome (IDMetAd)

  • IRAS ID

    349408

  • Contact name

    Justin Davies

  • Contact email

    justin.davies@uhs.nhs.uk

  • Clinicaltrials.gov Identifier

    24/PR/1240, REC reference number; PR committee, REC committee; 31/12/2024, Date of meeting

  • Duration of Study in the UK

    2 years, 0 months, 0 days

  • Research summary

    This proposal focuses on two imprinting disorders, Silver-Russell Syndrome (SRS) and Temple Syndrome (TS), both affecting pre- and postnatal growth and exposing to
    metabolic disturbances. The phenotype of SRS and TS patients is well described in children but not during adulthood. Since most adults with SRS and TS are not routinely followed, there is little information regarding the natural history of SRS and TS and the metabolic risks. The aim of this project is to build a cohort of SRS and TS patients for better transition and care in adulthood at a European level. Seven EU expert investigators in SRS and TS will join their efforts to identify a cohort of 100 adolescents and adults with a confirmed molecular diagnosis of SRS or TS. Each of the centres involved will recruit around 25 participants with SRS and TS patients of 16 years and older. Centralised serum and DNA banking will be organised in France to perform future ancillary studies. In this cohort we will collect clinical information as part of standard of care and assess the quality of life using questionnaires. The ultimate goal of this project will be to build European guidelines for transition of care for SRS and TS patients together with their management during adulthood and optimization of their care during childhood for a better outcome during adulthood.

  • REC name

    South Central - Hampshire A Research Ethics Committee

  • REC reference

    24/SC/0357

  • Date of REC Opinion

    18 Dec 2024

  • REC opinion

    Further Information Favourable Opinion