Study of Terguride Plus Symptomatic Therapy in patients with dcSSc

  • Research type

    Research Study

  • Full title

    Randomized, Multicenter, Double-Blind, Placebo-Controlled Trial to Evaluate the Efficacy and Safety of Terguride Plus Symptomatic Therapy in Subjects With Diffuse Cutaneous Systemic Sclerosis (TERGISS)

  • IRAS ID

    207414

  • Contact name

    Christopher Paul Denton

  • Contact email

    c.denton@ucl.ac.uk

  • Sponsor organisation

    medac GmbH

  • Eudract number

    2015-002586-39

  • Duration of Study in the UK

    3 years, 2 months, 10 days

  • Research summary

    Medac GmbH is conducting this study to investigate if a drug called Terguride is safe and effective in the treatment of diffuse cutaneous systemic sclerosis (dcSSc). dcSSC is an autoimmune disease of which outward signs are thickening and hardening of the skin. This form of the disease can also result in hardening of internal organs which can lead to problems in the lungs, kidneys, heart, digestive system, and other areas. \nAt present there are no approved drugs for the treatment of dcSSC and there is no cure. Current approved treatments are aimed at slowing progression and relieving symptoms. Terguride is approved in Japan for the treatment conditions related to excess prolactin. To date, over 200,000 people have been treated and side effects are known. A recent study showed that Terguride may be of benefit to people with dcSSc and further research is needed to confirm this.\nIn this study participants will receive Terguride as an oral tablet. For 12 months participants will receive either Terguride or placebo, neither patient or doctor will know which they are receiving. In the second year all participants will receive Terguride. Prior to both phases, participants will have 4 weeks of taking Terguride at different doses to determine the highest individually well-tolerated dose. Individuals metabolise Terguride differently therefore the total daily dose will be tailored to the participant.\nIt is expected that approximately 148 male and female participants, over 18 with dcSSC, will take part in this study worldwide with approximately 8 participants being recruited at 3 hospital sites in the UK. The duration of participation is expected to be 26.5 months with approximately 13 clinic visits and phone contacts between visits. Procedures include blood and urine samples, ECG, physical examinations, gynaecological examinations , patient diary and questionnaires. There are optional pharmacokinetic and skin biopsy sub-studies.\n\n

  • REC name

    London - Brighton & Sussex Research Ethics Committee

  • REC reference

    16/LO/1555

  • Date of REC Opinion

    18 Oct 2016

  • REC opinion

    Further Information Favourable Opinion