Stella-1 _ NHS-OBS-01

• Research type

  Research Study

• Full title

  A Multicenter, Prospective, Longitudinal, Observational Study in Children and Adults with Stargardt Disease Related Atrophy Secondary to Biallelic Mutations in the ABCA4 Gene

• IRAS ID

  354229

• Contact name

  Michel Michaelides

• Contact email

  michel.michaelides@ucl.ac.uk

• Sponsor organisation

  AAVantgarde Bio UK Limited

• Clinicaltrials.gov Identifier

  NCT06591806

• Duration of Study in the UK

  2 years, 1 months, 29 days

• Research summary

  This multicenter, prospective, longitudinal, observational study in subjects with Stargardt disease secondary to biallelic mutations in the ABCA4 gene aims to evaluate disease progression, characterize its structural and functional measures, and identify biomarkers for future interventional clinical studies.

• REC name

  Wales REC 4

• REC reference

  25/WA/0040

• Date of REC Opinion

  24 Mar 2025

• REC opinion

  Further Information Favourable Opinion