Stella-1 _ NHS-OBS-01

• Research type

  Research Study

• Full title

  A Multicenter, Prospective, Longitudinal, Observational Study in Children and Adults with Stargardt Disease Related Atrophy Secondary to Biallelic Mutations in the ABCA4 Gene

• IRAS ID

  346979

• Contact name

  Michel Michaelides

• Contact email

  michel.michaelides@ucl.ac.uk

• Sponsor organisation

  AAVantgarde Bio UK Limited

• Duration of Study in the UK

  2 years, 5 months, 29 days

• Research summary

  This multicenter, prospective, longitudinal, observational study in subjects with Stargardt disease secondary to biallelic mutations in the ABCA4 gene aims to evaluate prognostic factors of disease progression, and to further characterize the patient population for future clinical studies.

• REC name

  Wales REC 4

• REC reference

  24/WA/0256

• Date of REC Opinion

  31 Oct 2024

• REC opinion

  Further Information Favourable Opinion