RhuDex vs placebo in PBC

  • Research type

    Research Study

  • Full title

    Double-blind, randomised, placebo-controlled, phase II dose-finding study comparing different doses of RhuDex granules with placebo in the treatment of primary biliary cholangitis

  • IRAS ID

    289044

  • Contact name

    Michael Stieß

  • Contact email

    michael.stiess@drfalkpharma.de

  • Sponsor organisation

    Dr. Falk Pharma GmbH

  • Eudract number

    2020-001961-34

  • Duration of Study in the UK

    2 years, 3 months, 2 days

  • Research summary

    Researchers want to find out if the drug Rhudex can improve the disease Primary Biliary Cholangitis (PBC).
    Rhudex is an investigational (experimental) drug that is being tested and is currently not approved by any
    regulatory agency for sale. RhuDex is a novel, orally bioavailable, low molecular weight modulator of T-lymphocyte co-stimulation.

    This double-blind, randomised, multi-centre, placebo-controlled, comparative phase II trial will compare oral treatment with 50, 100 or 200 mg/day RhuDex granules vs placebo granules for the treatment of PBC.

    As all patients will continue standard of care treatment with UDCA, a placebo arm will be included as control due to regulatory recommendations to evaluate dose-related benefits and adverse effects in randomised, double-blind, placebo controlled studies.

    The study treatment duration will last 12 weeks ad each patient will have 7 study visits.

    The study has three main purposes:
    • To evaluate the efficacy of 3 doses of RhuDex vs placebo for the treatment of PBC in patients with an inadequate response to UDCA.
    • To identify efficacious RhuDex dose(s) for the treatment of PBC for further evaluation in phase III,
    • To study safety and tolerability of RhuDex.

    The study plans to enrol approximately 136 patients with PBC who are between the age of 18 and 74 years at up to
    60 centres in Europe.

  • REC name

    North East - Newcastle & North Tyneside 2 Research Ethics Committee

  • REC reference

    20/NE/0243

  • Date of REC Opinion

    7 Dec 2020

  • REC opinion

    Further Information Favourable Opinion