PKU Go - ACCEPTABILITY AND TOLERANCE

  • Research type

    Research Study

  • Full title

    PKU Go - ACCEPTABILITY AND TOLERANCE

  • IRAS ID

    222476

  • Contact name

    Anita MacDonald

  • Contact email

    anita.macdonald@bch.nhs.uk

  • Sponsor organisation

    Galen Ltd

  • Duration of Study in the UK

    0 years, 0 months, 15 days

  • Research summary

    The principle treatment for children with Phenylketonuria (PKU) is a low protein diet. Part of this treatment requires the administration of a protein substitute. Several brands of protein substitutes are already available in the UK in various\npresentations. However, compliance with taking protein substitutes continues to be a challenge. As a low protein diet is recommended for life, long term compliance is a growing concern. As a result, improving the choice in terms of product type may aid compliance.\nThis is a prospective, observational market research study in 15 children with PKU to evaluate the acceptability, tolerance and compliance with PKU-Go, a protein substitute for use in the dietary management of children with PKU over the age of 9 months.\nSubjects who are currently taking a protein substitute for PKU will be recruited for a 14-day trial of the new protein substitute to evaluate the tolerability and acceptability of the study product.\nDuring the 14-day trial caregivers will be asked to complete a daily questionnaire recording information on:\n• Usage and compliance\n• Ease of use and any issues with administration\n• Any gastro-intestinal side-effects.\nA questionnaire will also be completed at the beginning and end of the study that will consider perceptions about taste, appearance, smell, presentation and packaging of the product; ease of administration; how it is taken; and any other problems or symptoms.\nThe outcome of this assessment will be used in a submission to regulatory authorities to get the study product reimbursable on prescription in the UK.

  • REC name

    South West - Frenchay Research Ethics Committee

  • REC reference

    17/SW/0085

  • Date of REC Opinion

    13 Jun 2017

  • REC opinion

    Further Information Favourable Opinion