PIONEER-PKD

  • Research type

    Research Study

  • Full title

    A Phase I Randomised, Single-blind, Placebo-controlled Study to Assess the Safety, Tolerability, and Pharmacokinetics of AZD1613 Following Multiple Ascending Dose Administration in Participants with Autosomal Dominant Polycystic Kidney Disease

  • IRAS ID

    1012607

  • Contact name

    Roser Sanz Casañas

  • Contact email

    roser.sanz@astrazeneca.com

  • Sponsor organisation

    ASTRAZENECA FARMACÉUTICA SPAIN, S.A

  • Research summary

    This study is being conducted to learn more about an experimental drug called AZD1613 in participants who have autosomal dominant polycystic kidney disease (ADPKD), and also to better understand ADPKD and associated health problems. AZD1613 is expected to slow the progression of cyst formation and the decline in kidney function.

    This study will evaluate AZD1613 in comparison with placebo. Participants will take part in the study for about 33 weeks and will have up to 17 visits. Each visit may be different in length, from a short visit of around 1 hour to around 4 days, including overnight stays.

    About 40 patients will take part in this study globally including at 1 hospital in the UK.

  • REC name

    South Central - Oxford B Research Ethics Committee

  • REC reference

    25/SC/0287

  • Date of REC Opinion

    14 Nov 2025

  • REC opinion

    Further Information Favourable Opinion