Phase 1b/3 of Tazemetostat/Doxorubicin in Advanced Epithelioid Sarcoma

  • Research type

    Research Study

  • Full title

    A Phase 1b/3 Global, Randomized, Double-blind, Placebo-Controlled Trial of Tazemetostat in Combination With Doxorubicin as Frontline Therapy for Advanced Epithelioid Sarcoma

  • IRAS ID

    273166

  • Contact name

    Robin Jones

  • Contact email

    Robin.Jones@rmh.nhs.uk

  • Sponsor organisation

    Epizyme, Inc.

  • Eudract number

    2019-003648-55

  • Clinicaltrials.gov Identifier

    NCT04204941

  • Duration of Study in the UK

    8 years, 8 months, 5 days

  • Research summary

    Tazemetostat is a selective small inhibitor of the histone-lysine methyltransferase enzyme (a protein) EZH2 and is being developed as a treatment for patients with Epithelioid Sarcoma (ES), an ultra-rare and aggressive form of soft-tissue sarcoma (STS). Soft-tissue sarcomas represent only 1% of all cancer diagnoses, of which ES represent <1%.

    This is a global Phase 1b and Phase 3 Clinical trial, where approximately 154 patients are expected to be enrolled at 46 centres across North America, Europe and Asia-Pacific.

    The Phase 1b portion of the study is open-label (the patient and research team will know what drug the patient receives), designed to evaluate the effectiveness and safety of the combination of Tazemetostat and a approved cancer drug (Doxorubicin) and establish the recommended Phase 3 dose. The Phase 1b will consist of a screening, treatment and follow-up period. The treatment period will consist of dose-escalation with a starting dose of 400mg, followed by 600mg and then 800mg (Twice daily).

    The Phase 3 portion is double-blind (the patient or the research team will not know what treatment the patient receives), placebo controlled study designed to compare the effectiveness of Tazemetostat + Doxorubicin against the current standard treatment, Doxorubicin + Placebo. The Phase 3 portion consists of a screening, treatment and follow-up period. At the completion of the treatment period (disease progression) patients will be followed up every 12 weeks for at least 2 years.

  • REC name

    East of England - Cambridgeshire and Hertfordshire Research Ethics Committee

  • REC reference

    20/EE/0153

  • Date of REC Opinion

    17 Aug 2020

  • REC opinion

    Further Information Favourable Opinion