Patients-reported-outcome for Achalasia Symptom Score

  • Research type

    Research Study

  • Full title

    An International Patients-reported-outcome tool for Achalasia Symptom Score

  • IRAS ID

    267141

  • Contact name

    Sheraz Markar

  • Contact email

    s.markar@imperial.ac.uk

  • Sponsor organisation

    Imperial College London

  • Clinicaltrials.gov Identifier

    19SM5619,

  • Duration of Study in the UK

    1 years, 6 months, 2 days

  • Research summary

    Background:
    Achalasia is an oesophageal disease characterized by the absence of opening of the cardia at swallowing. Consequently, the food/liquid gets stuck in the gullet and patients experience dysphagia, regurgitation and chest pain. Treatment of achalasia consists of opening the cardia either by dilatation, surgery or paralysis of the muscle with botulinum toxin. Treatment efficacy is evaluated by symptom improvement, however, at present, there is no validated tool to objectively measure symptoms. To fill this gap we have developed a self-administered questionnaire through a Delphi consensus with 17 experts and refined it with cognitive interviews in 10 patients. We have calculated that to determine the threshold to define failure of a treatment as the 95th percentile of the lower score of non treated achalasia patients, we need to recruit 720 achalasia patients. The aims of this pilot study are to establish the acceptance rates of the questionnaire by patients and to capture the time needed to fill in the questionnaires of the study, in order to ultimately design a larger internationally based study.

    Methods:
    The questionnaire will be tested on fifty consecutive achalasia naive patients at Imperial College, UCL, Barts Health and King’s College NHS trusts. Questionnaires will be administered during the final visit before treatment, by a registered nurse that will record the agreement of patients to participate in the study and the time required to fill in the questionnaires- the I-Pass questionnaire, a questionnaire on quality of life (SF-36) and the Eckardt achalasia score (a non-validated, but widely used tool). Physiological data (manometry) and barium swallow results will be retrieved from the patient’s hospital chart.

    Patients who are neurologically impaired, have psychiatric problems or are not fluent in English will be excluded.

  • REC name

    East Midlands - Nottingham 1 Research Ethics Committee

  • REC reference

    20/EM/0167

  • Date of REC Opinion

    21 Jul 2020

  • REC opinion

    Further Information Favourable Opinion