Open Label Extension evaluating zagociguat in participants with MELAS

  • Research type

    Research Study

  • Full title

    An open-label extension study evaluating the safety of zagociguat in participants with MELAS who completed TIS6463-203

  • IRAS ID

    1011067

  • Contact name

    Wheatley Spence

  • Contact email

    wspence@tisentotx.com

  • Sponsor organisation

    Tisento Therapeutics, Inc.

  • Eudract number

    2024-517514-15

  • Clinicaltrials.gov Identifier

    NCT06961344

  • Research summary

    This study is an open label extension to allow participants from the TIS6463-203 study to continue taking zagociguat and assess its safety over a longer period. Zagociguat is being tested as a treatment for mitochondrial encephalomyopathy, lactic acidosis and strike-like episodes (MELAS) which can results in stroke like episodes, generalised fatigue . There is currently no approved treatment for MELAS. Participants will take a 15mg dose of zagociguat, daily, over a 104 week period. In-clinic visits will take place at 3 and 6 months following the first dose, with additional visits taking place at 6 month intervals; during these visits a number of assessments and questionnaires will be undertaken. Following the discontinuation of zagociguat, participants will have a follow up visit 4 weeks after.

  • REC name

    North East - Newcastle & North Tyneside 2 Research Ethics Committee

  • REC reference

    25/NE/0074

  • Date of REC Opinion

    29 May 2025

  • REC opinion

    Further Information Favourable Opinion