Mapping Disease Pathways of Biliary Atresia

  • Research type

    Research Study

  • Full title

    Mapping Disease Pathways of Biliary Atresia

  • IRAS ID

    233106

  • Contact name

    Anil Dhawan

  • Contact email

    anil.dhawan@nhs.net

  • Sponsor organisation

    Children's Hospital of Pittsburgh of UPMC

  • Duration of Study in the UK

    1 years, 10 months, 4 days

  • Research summary

    The overall objective of this proposal is to map developmental/genetic disease pathways for biliary atresia (BA), the most common cause of liver failure at birth, and the most common cause of liver transplantation in children, worldwide. The etiology of BA is not known. If known, novel preventive and management strategies may be devised to reduce the societal impact of this rare childhood disease, which is fatal without surgical correction. A second objective of this proposal is to determine whether candidate genes and related pathways which predispose to BA, also predispose to congenital heart disease, or vice versa. Stored liver tissue, of those patients with BA, will be sent to Children's Hospital of Pittsburgh in the United States for DNA and mRNA extraction and ultimately, analysis.

  • REC name

    London - City & East Research Ethics Committee

  • REC reference

    19/LO/1103

  • Date of REC Opinion

    27 Aug 2019

  • REC opinion

    Further Information Favourable Opinion