GW GWEP1560 NHIE CBD IV

  • Research type

    Research Study

  • Full title

    A Randomized, Double blind, Placebo controlled Single ascending Dose Trial to Evaluate the Safety, Tolerability, and Pharmacokinetics of GWP42003-P in Conjunction with Hypothermia in Neonates with Moderate or Severe Hypoxic Ischemic Encephalopathy

  • IRAS ID

    256518

  • Contact name

    Suresh Victor

  • Contact email

    suresh.victor@kcl.ac.uk

  • Sponsor organisation

    GW Research Ltd.

  • Eudract number

    2016-000936-17

  • Duration of Study in the UK

    1 years, 8 months, 24 days

  • Research summary

    Summary of Research

    Sometimes during birth, infants are stressed and don’t receive as much oxygen as they need (called asphyxia). When this happens, the infant may have brain injury. The presence of any brain injury at birth is called neonatal hypoxic ischemic encephalopathy (NHIE) and there can be long-term devastating consequences (for example; seizures and cerebral palsy). This study will investigate a new medication in infants diagnosed with NHIE that has been shown in animal studies to reduce brain injury after asphyxia. Infants will be considered for the study if they have moderate to severe NHIE and their doctor has decided to treat the infant by decreasing their body temperature with a cooling blanket, also known as therapeutic hypothermia. During the study four different doses of the medication will be given to determine the best and safest dose. The study will start at the lowest dose and only increase to a higher dose if the preceding dose is determined to be safe. Infants in the study will have blood drawn to determine the level of the study medication in their blood and to test for safety. The electrical activity in the infant’s brain will also be monitored by a non-invasive device on top of their head. Infants will be in the study during their entire stay in the neonatal intensive care unit (NICU). The parents will be asked to answer questions about seizures and development when the infant is 6 months and 1 year old. The primary part of the study will take place in NICUs in England and a total of 32 infants will participate in the study over a two-year study period.

    Summary of Results

    Conclusions:
    GWP42003-P was well tolerated, and there were no new or unexpected safety findings. The dose range of 0.1 to 1.0 mg/kg, administered IV for 15 minutes via continuous infusion in the participants, was not associated with complications, and all 13 participants (9 on GWP42003-P and 4 on placebo) achieved the protocol-defined target dose for the first 3 cohort groups, respectively.

    Link to results - https://eur03.safelinks.protection.outlook.com/?url=https%3A%2F%2Fu2790089.ct.sendgrid.net%2Fls%2Fclick%3Fupn%3DXv3JSvJ-2B3M71ppf7N9agba4yu73OCS9U-2BkKS40W1kfatiYvtk1-2B2gi1K6vKImual9G6VG4-2FeFhNKGHEnJKTVStcerk2OLhFa4EmeQgICvW75WNpCHDH8IFhVsBmKuy7ytxil_E1aO2-2BZlVOSJJV-2FajQqskegTd6IRomHYTi-2Fbt8SH3YLHDKSBO7yqaPbHrrY4kX02mSF07wkmJkS2hjs-2By7sbRuX09AKif54OtkGCGpwGMhK97cBWk4Jrb3-2BehISQz-2BRpbUza-2F9X0dUHGIqJwVJWicxuaYb8lWk5aDRmeNoU5crFpbiGAAUPgirkqejXMQoDDjRrKWuDfc4PNe7Wayok4Ew-3D-3D&data=05%7C01%7Capprovals%40hra.nhs.uk%7C28966a3e38ee4ecebb3b08daf4f063d9%7C8e1f0acad87d4f20939e36243d574267%7C0%7C0%7C638091610544948180%7CUnknown%7CTWFpbGZsb3d8eyJWIjoiMC4wLjAwMDAiLCJQIjoiV2luMzIiLCJBTiI6Ik1haWwiLCJXVCI6Mn0%3D%7C3000%7C%7C%7C&sdata=4YpRlNkt7Vr89ENdhkPw5su0vsDNal5sk8SAhZtIfoo%3D&reserved=0

  • REC name

    South Central - Berkshire B Research Ethics Committee

  • REC reference

    19/SC/0295

  • Date of REC Opinion

    23 Jul 2019

  • REC opinion

    Further Information Favourable Opinion