Gene Therapy Trial for Achromatopsia

• Research type

  Research Study

• Full title

  An Open-label, Single-site, Phase I/II Dose Escalation Trial of an Adeno-Associated Virus Vector (AAV2/8-hCARp-hCNGB3) for Gene Therapy of Adults and Children with Achromatopsia

• IRAS ID

  111087

• Contact name

  James Bainbridge

• Contact email

  j.bainbridge@ucl.ac.uk

• Sponsor organisation

  University College London, Joint Research Office

• Eudract number

  2012-003816-30

• ISRCTN Number

  n.a

• REC name

  London - West London & GTAC Research Ethics Committee

• REC reference

  12/LO/2008

• Date of REC Opinion

  22 Jan 2013

• REC opinion

  Further Information Favourable Opinion