Extension study of LUM001 in patients with PBC (CASCADE Study)

  • Research type

    Research Study

  • Full title

    An Open-label, Multicenter Extension Study to Evaluate the Long-term Safety and Tolerability of LUM001, an Apical Sodium-dependent Bile Acid Transporter Inhibitor (ASBTi), in Patients with Primary Biliary Cirrhosis

  • IRAS ID

    168030

  • Contact name

    Gideon Hirschfield

  • Contact email

    g.hirschfield@bham.ac.uk

  • Sponsor organisation

    Lumena Pharmaceuticals UK

  • Eudract number

    2014-003433-26

  • Duration of Study in the UK

    2 years, 7 months, 31 days

  • Research summary

    This is an open-label, multicenter study in adults with Primary Biliary Cirrhosis (PBC) designed to evaluate the long-term safety and tolerability of daily dosing with LUM001. LUM001 can stop bile acids from being absorbed from the gut into the body. It can lower the amount of bile acids in the blood and may reduce itching in people with primary biliary cirrhosis. This is an extension study to a current study, LUM001-201. For an individual subject, study participation will consist of a screening period of up to 4 weeks, followed by the treatment period which includes a 3-week dose escalation period. Subjects will continue dosing for up to 2 years, or until LUM001 is either commercially available or the Sponsor's decision to terminate the study.

  • REC name

    North East - York Research Ethics Committee

  • REC reference

    15/NE/0011

  • Date of REC Opinion

    15 Jan 2015

  • REC opinion

    Favourable Opinion