Examining the preferences of people with haemophilia for gene therapy

• Research type

  Research Study

• Full title

  examining the preferences of people with Haemophilia for Gene Therapy

• IRAS ID

  302902

• Contact name

  George Morgan

• Contact email

  george.morgan@hcdeconomics.com

• Sponsor organisation

  Pfizer

• Clinicaltrials.gov Identifier

  NA, NA

• Duration of Study in the UK

  0 years, 9 months, 27 days

• Research summary

  To investigate how patient preferences can be used in decision making and how they can be conducted in rare diseases. This study will investigate differences in preferences of people with haemophilia with varying levels of disease severity, for heamophilia treatments including gene therapy. It will consist of a Decision Choice Experiment where participants will choose 1 of 2 options within 14 hypothetical scenarios.

• REC name

  Wales REC 6

• REC reference

  21/WA/0271

• Date of REC Opinion

  14 Sep 2021

• REC opinion

  Further Information Favourable Opinion