Efficacy, Safety, and Tolerability of VLS-01-BU in Treatment Resistant Depression

  • Research type

    Research Study

  • Full title

    A Phase 2, Multicentre, Double-Blind, Randomised, Placebo-Controlled Trial to Assess the Efficacy, Safety, and Tolerability of Repeated Doses of VLS-01 Buccal Film in Participants with Treatment Resistant Depression.

  • IRAS ID

    1012312

  • Contact name

    Mary Shatzoff

  • Contact email

    Mary@atai.com

  • Sponsor organisation

    atai Therapeutics Inc.

  • Clinicaltrials.gov Identifier

    NCT06524830

  • Research summary

    This Phase 2 trial will determine the efficacy, safety, and tolerability of treatment with repeated doses of VLS-01 transmucosal buccal film (VLS-01-BU), which contains the active pharmaceutical ingredient and psychedelic N,N-dimethyltryptamine (DMT), in participants with treatment-resistant depression (TRD). The trial will also compare the onset and durability of antidepressant effects of VLS-01-BU versus placebo. The trial includes a 2-week placebo-controlled treatment period (Period 1), a 12-week placebo-controlled follow-up period (Period 2), and a 2-week non-placebo-controlled treatment and follow-up period (Period 3). Approximately 142 participants will be enrolled and randomised in a 1:1 ratio to receive a total of 2 placebo-controlled, double-blinded administrations of VLS-01-BU 120 mg or matching placebo, with a 2-week interval between each administration (Period 1). Participants will then be monitored for 12 weeks (Period 2) and then re-randomised in a 1:1 ratio to receive a third, double-blinded administration of VLS-01-BU 120 mg or VLS-01-BU 60 mg (Period 3). Participants will continute to be monitored for two weeks following this administration until the End of Study Visit (EOSV) for safety and to estimate the trajectory of their symptoms. VLS-01-BU (or placebo) will be delivered with standardised psychological support delivered by a trained healthcare provider. Trial participation will span up to 155 days and involve up to 17 visits, including a minimum of 9 in-clinic visits. Participants will complete various validated measures of symptoms and related functioning at each visit throughout the trial to help researchers understand the antidepressant effects, safety, and tolerability of VLS-01-BU in participants with TRD.

  • REC name

    London - Riverside Research Ethics Committee

  • REC reference

    25/LO/0408

  • Date of REC Opinion

    5 Aug 2025

  • REC opinion

    Further Information Favourable Opinion