Efficacy, PK, Safety and Tolerability of IGSC 20% in Subjects with PI

  • Research type

    Research Study

  • Full title

    A Multi-Center, Open-Label, Single-Arm Trial to Evaluate Efficacy, Pharmacokinetics, and Safety and Tolerability of IGSC 20% in Subjects with Primary Immunodeficiency

  • IRAS ID

    188274

  • Contact name

    Claire Bethune

  • Contact email

    claire.bethune@nhs.net

  • Sponsor organisation

    Grifols Therapeutics Inc.

  • Eudract number

    2015-003290-15

  • Duration of Study in the UK

    2 years, 2 months, 30 days

  • Research summary

    An investigation is being conducted to look into how safe and effective the study drug, IGSC 20% in subjects with Primary Immunodeficiency. Approximately 60 subjects will be enrolled so that approximately 20 adult subjects and 20 pediatric subjects are treated and complete the study. This study will include 3 study stages: Screening/Previous Regimen Phase, where subjects will be continue with their current IV or SC regimen; Treatment Stage 1, where subjects will receive 13 IGSC 20% doses weekly; and Treatment Stage 2 where subjects will receive 39 IGSC 20% doses weekly.\nA total of 52 doses of IGSC 20% will be administered with a final follow-up visit 1 week after the last dose at Week 53.

  • REC name

    Wales REC 3

  • REC reference

    16/WA/0046

  • Date of REC Opinion

    12 May 2016

  • REC opinion

    Further Information Favourable Opinion