DYNAMO

  • Research type

    Research Study

  • Full title

    The dynamic interplay between bleeding phenotype and baseline factor level in moderate and mild hemophilia A and B

  • IRAS ID

    248081

  • Contact name

    Anne-Fleur Zwagemaker

  • Contact email

    a.zwagemaker@amc.nl

  • Sponsor organisation

    R&D Office Manchester Royal Infirmary

  • Clinicaltrials.gov Identifier

    NCT03623295

  • Duration of Study in the UK

    1 years, 5 months, 1 days

  • Research summary

    Hemophilia is an inherited bleeding disorder caused by a deficiency of clotting factor VIII (hemophilia A) or factor IX (hemophilia B). People who have hemophilia A or B experience bleeds. The amount and the severity of the bleeds seem to coincide with the clotting factor VIII and IX levels. The relationship between the bleeding pattern and the clotting factor levels has been previously studied in hemophilia A and has shown variable results. There aren’t any studies known to have investigated this in hemophilia B. The DYNAMO study is an international study that is set up to gain insight in the association between clotting factor levels and the bleeding episodes in hemophilia A and B. This knowledge will also give us more insight in the onset and the expression of the different bleeding tendencies between hemophilia A and B. The DYNAMO study is being carried out by doctors and investigators at various hospitals. Patients with mild and moderate hemophilia A or B will be asked to participate. The study involves taking an extra blood sample. This blood will be used to look at the level of clotting factor levels at the moment of blood withdrawal. In addition, we will ask patients to fill in an online questionnaire about the bleeds they experienced in the past.

  • REC name

    North West - Greater Manchester South Research Ethics Committee

  • REC reference

    18/NW/0680

  • Date of REC Opinion

    19 Oct 2018

  • REC opinion

    Further Information Favourable Opinion