CTQJ230A12301E1 HORIZON OLE

  • Research type

    Research Study

  • Full title

    A single arm, multicenter, open-label extension (OLE) trial to evaluate long-term safety and tolerability of pelacarsen (TQJ230) in participants who completed the parent Lp(a)HORIZON trial

  • IRAS ID

    1011654

  • Contact name

    Fiona Morris

  • Contact email

    fiona.morris@novartis.com

  • Sponsor organisation

    Novartis Pharmaceuticals UK Ltd

  • Eudract number

    2024-519870-38

  • Research summary

    The purpose of this trial is to learn about the long-term treatment with TQJ230, also called pelacarsen, in people with cardiovascular disease and high levels of lipoprotein (a). This trial will include participants who have already completed the previous trial CTQJ230A12301.

    Cardiovascular disease (CVD) is a group of heart or blood vessel diseases in which the blood vessels that carry blood to the heart and other body parts become blocked. High blood levels of lipoprotein (a) [Lp(a)] can increase the chances of heart or blood vessel diseases like heart attack or stroke. TQJ230 is a trial drug that is being studied to reduce Lp(a) levels. It blocks the production of a protein called apolipoprotein (a) [apo(a)], which is required to produce Lp(a) in the body.
    Approximately 5,700 adult participants from all sexes and race are expected to join this trial. Based on the results of previous trials, TQJ230 may benefit people with CVD and high levels of Lp(a). This trial will benefit participants by providing TQJ230 after completing the CTQJ230A12301 trial.
    There might be medical problems with long term use of TQJ230 that are not yet known or have not been predicted. Participants will be closely monitored by the trial doctors for any such medical problems that may happen during the study.

  • REC name

    South Central - Berkshire B Research Ethics Committee

  • REC reference

    25/SC/0257

  • Date of REC Opinion

    30 Sep 2025

  • REC opinion

    Further Information Favourable Opinion