CRSP-ONC-002 CTX120 in Relapsed or Refractory Multiple Myeloma

  • Research type

    Research Study

  • Full title

    A Phase 1 Dose Escalation and Cohort Expansion Study of Safety and Efficacy of Anti-BCMA Allogeneic CRISPR-Cas9–Engineered T Cells (CTX120) in Subjects With Relapsed or Refractory Multiple Myeloma

  • IRAS ID

    273085

  • Contact name

    Rakesh Popat

  • Contact email

    rakesh.popat@ucl.ac.uk

  • Sponsor organisation

    CRISPR Therapeutics AG

  • Eudract number

    2019-002948-24

  • Clinicaltrials.gov Identifier

    NCT04244656

  • Duration of Study in the UK

    6 years, 2 months, 1 days

  • Research summary

    Research Summary:
    This study will evaluate the safety and efficacy, of CTX120 in patients with Multiple Myeloma (MM) that has relapsed or progressed.
    Chimeric antigen receptor (CAR) T cells are a form of cancer immunotherapy that have been used in the treatment of certain blood cancers. CTX120 is made from allogeneic (healthy donor) T cells that have been modified with CRISPR/Cas9 gene editing.
    This study will enrol male and female adult participants recruited form multiple global sites in various regions. There will be approximately 6 to 18 patients participating in Part A of the study. The study may be expanded to include approximately 70 additional patients in Part B. Participants will be enrolled in this study for approximately 5 years.
    After completion of this study, all participants will be required to enter a separate long-term follow-up study for an additional 10 years to assess safety and survival.
    Part A will assess the safety of increasing doses of CTX120 and will be used to determine the dose for Part B cohort expansion. Part B will assess the efficacy of CTX120 in relapsed or refractory MM.
    During both Part A and Part B, the study will consist of 3 main stages: 1. Screening, 2A+B. Lymphodepleting chemotherapy and subsequent infusion of CTX120 and Stage 3.5 year follow up.

    Lay summary of study results:
    26 patients with relapsed/refractory multiple myeloma were enrolled in Study CRSP-ONC-002 and treated with CTX120 at 5 different dose levels. CTX120 was well tolerated and there were no safety concerns. Partial responses were seen in 4 subjects.

  • REC name

    London - West London & GTAC Research Ethics Committee

  • REC reference

    20/LO/1085

  • Date of REC Opinion

    1 Dec 2020

  • REC opinion

    Further Information Favourable Opinion