CastleCreek - Diacerein Ointment - CCP-020-301

  • Research type

    Research Study

  • Full title

    An International, Multicenter, Randomized, Double-Blind, Parallel-Group Phase 2 Study Evaluating the Safety and Efficacy of Diacerein 1% Ointment Topical Formulation in Subjects with Epidermolysis Bullosa Simplex (EBS)

  • IRAS ID

    222887

  • Contact name

    Jemima Mellerio

  • Contact email

    jemima.mellerio@kcl.ac.uk

  • Sponsor organisation

    Castle Creek Pharmaceuticals, LLC

  • Eudract number

    2016-004427-24

  • Clinicaltrials.gov Identifier

    131, 384, IND Number

  • Duration of Study in the UK

    0 years, 10 months, 3 days

  • Research summary

    The study drug, Diacerein 1% Ointment is an investigational product being studied in the treatment of epidermolysis bullosa simplex (EBS).

    The study is being done to look at:
    • How well diacerein ointment works for the treatment of participants with EBS;
    • How safe and effective diacerein ointment is as compared to a placebo ointment.

    Diacerein in the topical formulation is broken down into "rhein" within the skin which is then absorbed into the blood stream. Rhein has shown to reduce the production of inflammatory proteins, which it does this in a way different to current non-steroid based drugs. This means it could be beneficial to those with EBS for whom current medication is not working.

    Up to 80 patients with EBS (of at least 4 years of age) in the US, Europe, Israel, and Australia will be recruited to take part in this study. Eligible patients will have a 50/50 chance of receiving the study drug or placebo. Patients will take part in this study and undergo tests for up to 22 weeks (up to 6 weeks screening, 8 weeks treatment and 8 weeks post-treatment follow-up).

  • REC name

    London - City & East Research Ethics Committee

  • REC reference

    17/LO/0882

  • Date of REC Opinion

    13 Jul 2017

  • REC opinion

    Further Information Favourable Opinion