ACCURACY STUDY

  • Research type

    Research Study

  • Full title

    ACCURACY study: a Phase 2, Open-Label, Single-Arm, Multi-Centre Study of AL101 in Patients with Adenoid Cystic Carcinoma (ACC) Bearing Activating Notch Mutations

  • IRAS ID

    262551

  • Contact name

    Robert Metcalf

  • Contact email

    robert.metcalf@christie.nhs.uk

  • Sponsor organisation

    Ayala Pharmaceuticals, Inc.

  • Eudract number

    2019-000309-64

  • Clinicaltrials.gov Identifier

    NCT03691207

  • Clinicaltrials.gov Identifier

    110,405, IND Number

  • Duration of Study in the UK

    1 years, 8 months, 17 days

  • Research summary

    Adult patients with adenoid cystic carcinoma (ACC) that is newly diagnosed, has come back or did not get better with their last therapy and who have alterations in a group of genes called Notch will be recruited for the study.
    Notch is a gene present in normal cells but when there are changes or mutations in this gene, it causes the cells to behave differently and enables them to form tumours. Too much Notch activity induces cells to divide out of control.
    AL101 is an experimental drug and we are studying AL101 to find out what its side effects are and if it works for ACC. AL101 works by blocking excessive Notch activity and induces the death of the tumour cells. This study is designed to test whether this is true.
    If the patient consents to take part and the study doctor decides they can be in the study, AL101 will be given 4 mg intravenously (IV) weekly. The infusion will take approximately 1 hour.
    The patient will be treated using this schedule:
    - An infusion once a week on Days 1, 8, 15 and 22 of each 28-day cycle.
    - Cycle 1 Day 1 is considered the first time the patient will get the AL101 infusion.
    - Every 28 days is considered study-cycle.

    The patient will also undergo regular study assessments and procedures including radiographic imaging to understand if the tumour is responding to therapy with AL101. If the drug is killing the tumour cells, then the size of the tumour will decrease.
    All the study assessments and procedures including AL101 administration will place at the study hospital
    Approximately 36 volunteers will take part in this study globally.

  • REC name

    North West - Greater Manchester Central Research Ethics Committee

  • REC reference

    19/NW/0660

  • Date of REC Opinion

    24 Oct 2019

  • REC opinion

    Favourable Opinion