A study of paediatric patients with non-Hodgkins lymphoma

  • Research type

    Research Study

  • Full title

    A Phase II, single arm, multicentre, open label trial to determine the safety and efficacy of tisagenlecleucel in paediatric patients with relapsed or refractory mature B-cell non-Hodgkin lymphoma (NHL).

  • IRAS ID

    253086

  • Contact name

    Sara Ghorashian

  • Contact email

    Sara.Ghorashian@gosh.nhs.uk

  • Sponsor organisation

    Novartis Pharmaceuticals UK Ltd

  • Eudract number

    2017-005019-15

  • Clinicaltrials.gov Identifier

    EMEA-001654-PIP02-17,

  • Duration of Study in the UK

    3 years, 6 months, 11 days

  • Research summary

    This is an open-label, single arm 2 year study, the purpose of which is to test an experimental approach called modified T-cell therapy, to see if it is safe and will help with the treatment of children and adolescents with non-Hodgkins lymphoma(NHL). In this study, T cells (a type of white blood cell) will be removed from the patient's blood using a process called 'leukapheresis', modified in order to target the lymphoma, and then returned back to them. The T cells will be changed in a way that can allow them to identify and possibly kill the patient’s NHL tumour cells.
    The modification of the T cells is done by a process called gene transfer which results in a genetic modification to the T cells taken from the patient's body. These modified T cells are called tisagenlecleucel cells and they will be administered to the patient by intravenous infusion approximately six weeks later. Patients then enter a follow up period of around two years during which they have regular blood tests performed and well as ongoing assessment of their disease status.

  • REC name

    South Central - Oxford A Research Ethics Committee

  • REC reference

    19/SC/0375

  • Date of REC Opinion

    4 Nov 2019

  • REC opinion

    Further Information Favourable Opinion