19580 aTFPI

  • Research type

    Research Study

  • Full title

    Multiple escalating dose study of BAY 1093884 in adults with Haemophilia A or B with or without inhibitors.

  • IRAS ID

    240062

  • Contact name

    Charles Hay

  • Contact email

    charles.hay@cmft.nhs.uk

  • Sponsor organisation

    Bayer AG

  • Eudract number

    2017-003324-67

  • Duration of Study in the UK

    1 years, 7 months, 12 days

  • Research summary

    This is an open-label, phase 2 study with multiple escalating subcutaneous doses of BAY 1093884 in adults (age≥ 18 years) with Haemophilia A or B with or without inhibitors.

    The primary objective is to evaluate the safety and tolerability of BAY 1093884.

    Exploratory objectives: pharmacokinetics (PK) and pharmacodynamics (PD) of BAY 1093884 and the effect of different doses of BAY 1093884 in bleeding control.

    Major Inclusion criteria:
    • Male subjects with Haemophilia A or Haemophilia B (any severity) with inhibitors against FVIII or FIX (any inhibitor titer).
    • Male subjects with severe Haemophilia A (FVIII activity <1%) or B (FIX activity <2%) without inhibitors.
    • Subjects with a past history of inhibitors (any inhibitor titer) are eligible.

    Major exclusion criteria
    • History of any other coagulation disorder (particularly disseminated intravascular coagulopathy or combined FVIII/FV deficiency) or platelet disorder.
    • History of diseases related to venous thromboembolic events (e.g., pulmonary embolism, deep vein thrombosis, and thrombophlebitis) or thrombotic microangiopathy.
    • Risk factors for venous or arterial diseases (e.g., uncontrolled hypertension, uncontrolled diabetes).
    • History of cardiac, coronary and/or arterial peripheral atherosclerotic disease, particularly myocardial infarction, cerebrovascular accident, stroke, transient ischemic attack, congestive heart failure, angina pectoris or treatment for angina pectoris.

  • REC name

    London - Central Research Ethics Committee

  • REC reference

    18/LO/0656

  • Date of REC Opinion

    22 Jun 2018

  • REC opinion

    Further Information Favourable Opinion